{"id":1434,"date":"2019-03-25T23:16:08","date_gmt":"2019-03-25T22:16:08","guid":{"rendered":"https:\/\/www.glycogenoses.org\/?p=1434"},"modified":"2019-03-25T23:20:04","modified_gmt":"2019-03-25T22:20:04","slug":"maladie-de-pompe-prevention-de-limmunite-anti-gaa-dans-un-modele-murin","status":"publish","type":"post","link":"https:\/\/www.glycogenoses.org\/st_qlfctn\/maladie-de-pompe-prevention-de-limmunite-anti-gaa-dans-un-modele-murin\/","title":{"rendered":"Maladie de Pompe : pr\u00e9vention de l&rsquo;immunit\u00e9 anti-GAA dans un mod\u00e8le murin"},"content":{"rendered":"\n<p>Th\u00e9rapie g\u00e9nique : Une strat\u00e9gie de th\u00e9rapie g\u00e9nique permet de pr\u00e9venir la r\u00e9action immunitaire anti-GAA et entra\u00eene une expression durable de la prot\u00e9ine dans des souris d\u00e9ficientes en GAA. <br><a href=\"https:\/\/www.afm-telethon.fr\/actualites\/maladie-pompe-prevention-immunite-anti-gaa-dans-modele-murin-127181\">Pour en savoir plus (site AFM-Telethon)<\/a><\/p>\n\n\n\n<p><strong>Source<\/strong><br> AAV Gene Transfer with Tandem Promoter Design Prevents Anti-transgene Immunity and Provides Persistent Efficacy in Neonate Pompe Mice.<br> Colella P, Sellier P, Costa Verdera H, Puzzo F, van Wittenberghe L, Guerchet N, Daniele N, Gjata B, Marmier S, Charles S, Simon Sola M, Ragone I, Leborgne C, Collaud F, Mingozzi F.<br> Mol Ther Methods Clin Dev. 2018 Nov 17<\/p>\n","protected":false},"excerpt":{"rendered":"<p>Th\u00e9rapie g\u00e9nique : Une strat\u00e9gie de th\u00e9rapie g\u00e9nique permet de pr\u00e9venir la r\u00e9action immunitaire anti-GAA et entra\u00eene une expression durable de la prot\u00e9ine dans des souris d\u00e9ficientes en GAA. Pour en savoir plus (site AFM-Telethon) Source AAV Gene Transfer with Tandem Promoter Design Prevents Anti-transgene Immunity and Provides Persistent Efficacy in Neonate Pompe Mice. ColellaLeer M\u00e1s<\/p>\n","protected":false},"author":7,"featured_media":1106,"comment_status":"closed","ping_status":"open","sticky":false,"template":"","format":"standard","meta":[],"categories":[19,14],"tags":[],"_links":{"self":[{"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/posts\/1434"}],"collection":[{"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/users\/7"}],"replies":[{"embeddable":true,"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/comments?post=1434"}],"version-history":[{"count":2,"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/posts\/1434\/revisions"}],"predecessor-version":[{"id":1436,"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/posts\/1434\/revisions\/1436"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/media\/1106"}],"wp:attachment":[{"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/media?parent=1434"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/categories?post=1434"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.glycogenoses.org\/st_qlfctn\/wp-json\/wp\/v2\/tags?post=1434"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}